The Two Year Mark
This Saturday Marian and I are flying to Maryland to attend the Patient Focused Drug Development Meeting for Niemann-Pick Type C. I, along with several other families, am speaking and sharing Marian's story with representatives from the FDA and the other hundred forty plus families, scientists, doctors and pharmaceutical companies in attendance. Not to mention anyone who wants to register to watch the live stream. No pressure. I guess if I made it through a live news segment