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Help Us Save
Children & Adults
Fighting
Niemann-Pick Type C
NPC IS DEVASTATING.
IT IS ALWAYS FATAL, STRIKING ANY AGE FROM INFANTS TO ADULTS.
MOST PATIENTS HAVE NO FAMILY HISTORY.
THERE IS NO CURE AND ACCESS TO LIMITED THERAPIES ARE RESTRICTIVE. WE ARE WORKING TO CHANGE THIS.
WE GIVE A VOICE TO PATIENTS AROUND THE WORLD ADVOCATING UNIVERSAL ACCESS FOR LIFE SUSTAINING MEDICINES FOR THIS GENERATION OF CHILDREN AND ADULTS FIGHTING NPC.
A BRIEF LOOK AT AN NPC DIAGNOSIS


Children and adults are in the fight of their lives against fatal Niemann-Pick Type C. Without treatment and a cure they will lose their ability to move, speak, eat, breathe and live.
This disease strikes all ages, most frequently children. It's the short term memory loss of Alzheimer's, the tremors of Parkinson's and the systemic decline of ALS. Two experimental medications that patients rely on to slow the disease are at risk of being taken away.
They need your help to stay alive.
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Ways You Can Help

DONATE
Your donation will support patient access to medication and information as well as treatment research and development.

CURRENT INITIATIVES
Educating yourself on our current initiatives will help keep you up-to-date on the ever-changing landscape of treatment.

OUR STORIES
Reading stories of the people and their families who are affected by NPC will help you to understand what they are facing.

Hope for Marian
Sara and Paul McGlocklin started Hope for Marian after their second daughter, Marian, was diagnosed with Niemann-Pick Type C in 2017. Read about their journey through Sara's blog, and the foundation's mission.
